Start, switch and stop (triple-S) criteria for enzyme replacement therapy of late-onset Pompe disease: European Pompe Consortium recommendation update 2024.
Schoser B, van der Beek N, Broomfield A, Brusse E, Diaz-Manera J, Hahn A, Hundsberger T, Kornblum C, Kruijshaar M, Laforet P, Mengel E, Mongini T, Orlikowski D, Parenti G, Pijnappel W, Roberts M, Scherer T, Toscano A, Vissing J, O'Sullivan J, van Doorn P, Wenninger S, van der Ploeg A. Start, switch and stop (triple-S) criteria for enzyme replacement therapy of late-onset Pompe disease: European Pompe Consortium recommendation update 2024. Eur J Neurol 2024; 31:e16383.
Jun 14, 2024
Start, switch and stop (triple-S) criteria for enzyme replacement therapy of late-onset Pompe disease: European Pompe Consortium recommendation update 2024.
Jun 14, 2024
Eur J Neurol 2024; 31:e16383
Schoser Benedikt, van der Beek Nadine A M E, Broomfield Alexander, Brusse Esther, Diaz-Manera Jordi, Hahn Andreas, Hundsberger Thomas, Kornblum Cornelia, Kruijshaar Michelle E, Laforet Pascal, Mengel Eugen, Mongini Tiziana, Orlikowski David, Parenti Giancarlo, Pijnappel W W M Pim, Roberts Mark, Scherer Thomas, Toscano Antonio, Vissing John, O'Sullivan Joe M, van Doorn Pieter A, Wenninger Stephan, van der Ploeg Ans T
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